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ASH 2021 — LentiGlobin improves quality of life up to 24 months in sickle cell disease.

Daniela Ovadia — Agenzia Zoe | Conference Report | 16 December 2021

A gene therapy treatment could bring long-lasting quality of life to sickle cell disease patients

by Massimo Sandal (Agenzia Zoe)

Takeaway messages

LentiGlobin gene therapy improves quality of life (QoL), pain and fatigue in sickle cell disease (SCD) up to 24 months after treatment.

Why this matters

ASH 2021

Depression

General Medicine

Genomic Medicine

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Quiz challenge Emerging diseases: COVID-19

Closed 10 Questions Available Ends on 1 October 2020

ESMO 2020 topic challenge

Closed 5 Questions Available Ends on 21 April 2021

Women's health challenge

Closed 10 Questions Available Ends on 12 May 2021

Antibiotics - Consequence of MDR carriage

Closed 6 Questions Available Ends on 12 May 2021

Neurological disorders challenge

Closed 10 Questions Available Ends on 12 June 2021

Rheumatology challenge

Closed 10 Questions Available Ends on 12 July 2021

Lyme Disease

Closed 11 Questions Available Ends on 12 July 2021

Mental health challenge

Closed 10 Questions Available Ends on 12 August 2021

Topic challenge - Children conditions

Closed 7 Questions Available Ends on 12 September 2021

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ASH 2021 — LentiGlobin improves quality of life up to 24 months in sickle cell disease.

March Challenge

Which of these bacterial species can cause a tick-borne relapsing fever?

What are the causes of an adult-acquired flatfoot deformity?

Are Listeria outbreaks linked to imported food items?

What is the most common condition for foetal stillbirths in South Asia?

How to classify nasoorbitoethmoid fractures?

Hypertension: How safe is your sight?

What are the risk factors for age-related macular degeneration?

How do you therapeutically manage inferiority complex disorder?

What are the causes of intrinsic restrictive lung diseases?

What do we know about acute flaccid paralysis?

What is not a criterion in the ADA risk scoring for thrombosis in patients with COVID-19?

What pathology can alpha-synuclein malformation cause?

Which of the following is not true about diabetic nephropathy?

Which is not a policy document of the World Medical Association?

What is not a contraceptive option for women at high risk for HIV infection?

What is an anterior and posterior approach for cervical spondylotic myelopathy?

Which beta-blocker is more suitable for managing LQTS and CPVT?

Chapare virus is endemic to which of the following countries?

Which mutation is responsible for Klippel-Trénaunay syndrome?

Can you identify the right GOLD grade for a patient with COPD?

Topic Challenges

Quiz challenge Emerging diseases: COVID-19

ESMO 2020 topic challenge

Women's health challenge

Antibiotics - Consequence of MDR carriage

Neurological disorders challenge

Rheumatology challenge

Lyme Disease

Mental health challenge

Topic challenge - Children conditions

Lyme Disease