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Fatal cases of liver injury with spinal muscular atrophy gene therapy

Medical News   |   19 January 2023
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The European Medicines Agency (EMA) has issued a safety alert regarding the first gene therapy for spinal muscular atrophy (SMA), which was authorised by the EMA less than 3 years ago.

The agency says it has recently received reports of two fatal cases of acute liver failure in patients with...

          

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